文章基本信息

标题：Response to Gurevich and colleagues: The effect of enzyme replacement therapy on clinical outcomes in male patients with Fabry disease: a systematic literature review by a European panel of experts
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作者：Dominique P. Germain ; Bruno Falissard ; Max J. Hilz 等
期刊名称：Molecular Genetics and Metabolism Reports
印刷版ISSN：2214-4269
出版年度：2019
卷号：20
页码：1-2
DOI：10.1016/j.ymgmr.2019.100493
出版社：Elsevier B.V.
关键词：Fabry disease ; Enzyme replacement therapy ; Agalsidase alfa ; Agalsidase beta